Join Mailing List   |   Jobs   |   Print Page   |   Contact Us   |   Sign In   |   Join
Hemophilia Gene Therapy- Learning from Clinical Trials and Preparing for Clinical Practice
Tell a Friend About This EventTell a Friend
 

8/5/2020
When: Wednesday, August 5, 2020
11:00

« Go to Upcoming Event List  

With the expected approval of the first gene therapy drugs for hemophilia in the next few months, it is important to clinicians are prepared for implementation in their respective hemophilia treatment centers (HTCs). During this 90-minute session, Drs. Steven Pipe and Guy Young will provide an overview of gene therapy for treatment of hemophilia along with an update on clinical trials on Hemophilia A and B. They will also discuss what success looks like and how HTCs should be preparing for the advent of gene therapy. The presentation will conclude with a live question and answer session between attendees and Drs. Pipe and Young. 

Register Here

Agenda 

7:00-7:05: Welcome and Introductions

7:05-7:20: Overview of Gene Therapy of Hemophilia: Vector and Transgene Optimization

7:20-7:35: Update on Clinical Trials of Gene Therapy in Hemophilia A and Hemophilia B

7:35-7:50: What does Success Look Like? Outcomes Behind Clinical Trial Endpoints 

7:50-8:10: What does Readiness Look Like? Peparing HTCs for Gene Therapy

8:10-8:30: Question and Answer Session

 

Supported through educational grants from BioMarin, Freeline Therapeutics Limited, Pfizer Inc., Shire, Spark Therapeutics and uniQure, Inc.

Membership Management Software Powered by YourMembership  ::  Legal
This website uses cookies to store information on your computer. Some of these cookies are used for visitor analysis, others are essential to making our site function properly and improve the user experience. By using this site, you consent to the placement of these cookies. Click Accept to consent and dismiss this message or Deny to leave this website. Read our Privacy Statement for more.