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News & Press: Press Releases

ISTH Announces Its Launch of New Global Education Initiative in Gene Therapy for Hemophilia

Friday, July 5, 2019   (0 Comments)
Posted by: Luke Blount
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MELBOURNE – July 6, 2019 – The International Society on Thrombosis and Haemostasis (ISTH) is pleased to announce the official launch of Gene Therapy in Hemophilia: An ISTH Education Initiative. This landmark launch, the first of its kind in Hemophilia, will take place during the ISTH XXVII Congress, also known as ISTH 2019, held in Melbourne, Australia, July 6-10, 2019. 

As gene therapy emerges as a potential new treatment for patients with hemophilia, the ISTH recognizes an immediate need to educate clinicians and scientists in the global hemophilia healthcare community. In early 2019, the ISTH organized the ISTH Gene Therapy for Hemophilia Steering Committee, a group of world-renowned experts, led by Flora Peyvandi, M.D., Ph.D., and David Lillicrap, M.D., to survey the global hemophilia healthcare community to identify unmet educational needs specific to gene therapy in hemophilia.

The detailed survey results will be presented in a poster session in Melbourne on July 7, titled, “Gene Therapy Knowledge and Perceptions: Results of an International ISTH Survey.” It will also be presented during the Product Theater Sessions on July 7 at 12:15 p.m. The ISTH Gene Therapy for Hemophilia Steering Committee utilized the results of the survey, with input from others, to design a dynamic educational roadmap to guide the evolution of the gene therapy education program.

The aim in 2019 is to raise awareness and to provide clinicians and scientists with a better understanding of the fundamentals of gene therapy, the treatment approach, research and clinical trials, safety and efficacy outcomes, how to identify patients who could benefit, and how to analyze implications of this new treatment approach. The educational roadmap will also prepare the global hemophilia community for the possibility of new treatments for hemophilia.

“Launching the roadmap in Melbourne is an exciting opportunity to kick off this global education initiative. It is an important first step in educating clinicians and researchers about the science and potential role of gene therapy for patients with hemophilia,” said ISTH President Claire McLintock. “Our leadership in the steering committee and feedback from the greater thrombosis and hemostasis community has allowed us to understand the current needs and create meaningful education in gene therapy for the ISTH global hemophilia community.”

“With the treatment landscape in hemophilia rapidly evolving and clinicians around the world being challenged to keep current with the latest scientific developments and clinical advancements, developing state-of-the-art clinical practice guidelines and education programs is critical to ensure best patient care,” said Flora Peyvandi, MD, PhD, Co-Chair of the ISTH Gene Therapy for Hemophilia Steering Committee.

Gene Therapy in Hemophilia: An ISTH Education Initiative is supported by educational grants from BioMarin, Pfizer, Inc., Shire, Spark Therapeutics, and uniQure, Inc. For more information, visit


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About the ISTH
Founded in 1969, the ISTH is the leading worldwide organization dedicated to advancing the understanding, prevention, diagnosis and treatment of conditions related to thrombosis and hemostasis. ISTH is an international professional membership organization with more than 5,000 clinicians, researchers and educators working together to improve the lives of patients in more than 100 countries around the world. Among its highly regarded activities and initiatives are education and standardization programs, research activities, meetings and congresses, peer-reviewed publications, expert committees and World Thrombosis Day on 13 October. Visit ISTH online at

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